FRIDAY, APRIL 13 7:00 PM - 9:30 PM
Meet and Greet Reception for all presenters, attendees, and guests Cabrillo Salon 1
SATURDAY, APRIL 14 8:00 AM
Breakfast Available Welcome Address
8:15 AM - 8:45 AM
Cabrillo Ballroom 12
8:45 AM - 9:15 AM
Cabrillo Ballroom 12
• What do we know about Duchenne • Genotype/phenotype • Predicting Progression
9:15 AM - 9:45 AM
Cabrillo Ballroom 12
• The interdisciplinary model – who is involved • Baseline tests to consider and frequency • Pediatric through Transition care
9:45 AM - 10:15 AM
Cabrillo Ballroom 12
10:15 AM - 10:30 AM
Q&A and Break
10:30 AM - 11:00 AM
Cabrillo Ballroom 12
11:00 AM - 11:30 AM
Cabrillo Ballroom 12
11:30 AM - 12:00 PM
Cabrillo Ballroom 12
12:00 PM - 12:15 PM
Q&A
12:15 PM - 1:15 PM
Lunch
1:20 PM - 1:50 PM
Cabrillo Ballroom 12
1:50 PM - 2:00 PM
Cabrillo Ballroom 12
Natural History
Caring for Duchenne
Understanding Endocrine
Elements of Cardiac Care
Pat Furlong, PPMD President
Craig McDonald, MD
Kathryn Wagner MD, PhD
Alan Rogol, MD
Ron Victor, MD
Behaviors in Duchenne
James Poysky, PhD
Pulmonary Management
Joshua Benditt, MD
Duchenne Research: Understanding the Strategies
Jasbir Seehra, PhD
Introduction to Clinical Trials Discussions
Jasbir Seehra, PhD
SATURDAY, APRIL 14 (continued) Steroid Approaches
2:00 PM - 2:30 PM
Cabrillo Ballroom 12
• NFKappa B • Delta 9,11 • others
2:30 PM - 3:00 PM
Cabrillo Ballroom 12
• Myostatin • Folistatin • others
Compounds and Biologics in Development
Cabrillo Ballroom 12
• Prosensa • AVI • GSK
3:30 PM - 4:00 PM
Q&A and Break
4:00 PM - 4:30 PM
Cabrillo Ballroom 12
• Ataluren • others
• PTC Molecule • Summit • others
Cabrillo Ballroom 12
• Beta Blockers • Active Load Approaches • others
5:30 PM - 6:00 PM
Lee Sweeney, PhD
Cardiac Approaches
5:00 PM - 5:30 PM
Craig McDonald, MD
Utrophin Upregulation
Cabrillo Ballroom 12
Nagaraju Kanneboyina, PhD
Stop Codon Read Thru
4:30 PM - 5:00 PM
Kathryn Wagner, MD, PhD
Exon Skipping
3:00 PM - 3:30 PM
Nagaraju Kanneboyina, PhD
Linda Cripe, MD
Q&A and Closing Remarks
SUNDAY, APRIL 15 7:45 AM - 9:00 AM
Breakfast Available
8:00 AM - 9:15 AM
Documentary Screening - Duchenne With A Future: The Power to Live
A documentary discussing success factors in Duchenne
9:30 AM - 11:30 AM
9:30 AM
Cabrillo Ballroom 12
Harbor Ballrooms A-E
Breakout Sessions Santa Fe 3
Santa Fe 4
HerSelf First - Session 1
Behavior
HerSelf First - Session 2
Enhancing Your Son’s School Experience
Sheila Moeschen, PhD
10:30 AM
Sheila Moeschen, PhD
James Poysky, PhD
Jill Castle